{"id":6737,"date":"2021-12-01T07:15:10","date_gmt":"2021-12-01T12:15:10","guid":{"rendered":"https:\/\/www.med.unc.edu\/neuroscience\/?p=6737"},"modified":"2021-12-01T07:15:10","modified_gmt":"2021-12-01T12:15:10","slug":"one-shot-gene-therapy-for-angelman-syndrome-shows-promise-in-mice","status":"publish","type":"post","link":"https:\/\/www.med.unc.edu\/neuroscience\/one-shot-gene-therapy-for-angelman-syndrome-shows-promise-in-mice\/","title":{"rendered":"One-shot gene therapy for Angelman syndrome shows promise in mice"},"content":{"rendered":"<p>One injection of a potential new\u00a0gene therapy for Angelman syndrome\u00a0forestalls many of the neurodevelopmental condition\u2019s key traits, according to early tests in mice.<\/p>\n<p>\u201cWhile additional pharmacology and safety studies are needed, our viral vector can potentially provide transformative therapeutic relief with a single dose,\u201d says lead investigator\u00a0Benjamin Philpot, professor of neuroscience at the University of North Carolina at Chapel Hill.<\/p>\n<p>Full article can be found on the <a href=\"https:\/\/www.spectrumnews.org\/news\/one-shot-gene-therapy-for-angelman-syndrome-shows-promise-in-mice\/\" target=\"_blank\" rel=\"noopener\">Spectrum News Website<\/a>.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>One injection of a potential new\u00a0gene therapy for Angelman syndrome\u00a0forestalls many of the neurodevelopmental condition\u2019s key traits, according to early tests in mice. \u201cWhile additional pharmacology and safety studies are needed, our viral vector can potentially provide transformative therapeutic relief with a single dose,\u201d says lead investigator\u00a0Benjamin Philpot, professor of neuroscience at the University of &hellip; <a href=\"https:\/\/www.med.unc.edu\/neuroscience\/one-shot-gene-therapy-for-angelman-syndrome-shows-promise-in-mice\/\" aria-label=\"Read more about One-shot gene therapy for Angelman syndrome shows promise in mice\">Read more<\/a><\/p>\n","protected":false},"author":7858,"featured_media":6361,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"footnotes":"","_links_to":"","_links_to_target":""},"categories":[2],"tags":[],"class_list":["post-6737","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-news","odd"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v26.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>One-shot gene therapy for Angelman syndrome shows promise in mice | UNC Neuroscience Center<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/www.med.unc.edu\/neuroscience\/one-shot-gene-therapy-for-angelman-syndrome-shows-promise-in-mice\/\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"One-shot gene therapy for Angelman syndrome shows promise in mice | UNC Neuroscience Center\" \/>\n<meta property=\"og:description\" content=\"One injection of a potential new\u00a0gene therapy for Angelman syndrome\u00a0forestalls many of the neurodevelopmental condition\u2019s key traits, according to early tests in mice. \u201cWhile additional pharmacology and safety studies are needed, our viral vector can potentially provide transformative therapeutic relief with a single dose,\u201d says lead investigator\u00a0Benjamin Philpot, professor of neuroscience at the University of &hellip; Read more\" \/>\n<meta property=\"og:url\" content=\"https:\/\/www.med.unc.edu\/neuroscience\/one-shot-gene-therapy-for-angelman-syndrome-shows-promise-in-mice\/\" \/>\n<meta property=\"og:site_name\" content=\"UNC Neuroscience Center\" \/>\n<meta property=\"article:published_time\" 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