The National MPS Society will host a timed 5K run and 1 mile walk, beginning at 9 AM on Saturday, March 28. The 1 mile walk will begin at 9:05 AM. Packet pickup and day of registration will open at 7:30 AM. A picnic for attendees and volunteers will be held after the race! This … Read more
Uplifting Athletes is a national nonprofit that harnesses the power of sport to invest in the lives of individuals and families impacted by rare disease (both children and adults). They are excited to invite rare individuals and families to join us for a one-of-a-kind bowling event at Bowlero Durham with the UNC Football Team on … Read more
Advancing treatments for rare diseases requires innovative ways to measure success. Join FDA, researchers, clinicians, and innovators for a free, one-day virtual workshop open to the public focused on emerging scientific and regulatory pathways for advancing surrogate endpoints in rare disease drug development. This workshop is being convened in support of the Rare Disease Endpoint … Read more