May 12, 2022
Philpot Lab published in eLife
Restoring lost gene activity prevents many disease signs in an animal model of the rare, single-gene neurodevelopmental condition. The UNC Neuroscience Center lab of Ben Philpot, PhD, led this research. Article: https://elifesciences.org/articles/72290 UNC press release: https://news.unchealthcare.org/2022/05/gene-therapy-could-treat-pitt-hopkins-syndrome-proof-of-concept-study-suggests/