UNC School of Medicine scientists are researching gene therapy for Angelman Syndrome
June 29, 2020
UNC School of Medicine researchers Drs. Mark Zylka and Ben Philpot are partnering with AskBio to develop a gene therapy treatment for Angelman syndrome, a rare neurogenetic disorder with no cure. Preclinical evidence has shown that gene therapy may improve motor outcomes and reduce seizures, potentially transforming the lives of...